O42: Development of an anti-sense oligonucleotide therapeutic targeting RhoBTB2-related epileptic encephalopathy

Bibliographic Details
Title: O42: Development of an anti-sense oligonucleotide therapeutic targeting RhoBTB2-related epileptic encephalopathy
Authors: Wheeler, Matthew, Bonner, Devon, Alvarez, Raquel, Emami, Sara, Coca, Richard, Willis, Brandon, Mendez, Hector, Patel, Ruchi, Duong, Kate, Arthur, Jennifer, Karakikes, Ioannis, Bernstein, Jonathan, Porter, Brenda, Knowles, Juliet, Lloyd, Kent, LaRocca, Thomas
Source: In Genetics in Medicine Open 2024 2 Supplement 1
Database: ScienceDirect
More Details
ISSN:29497744
DOI:10.1016/j.gimo.2024.101025
Published in:Genetics in Medicine Open
Language:English