O42: Development of an anti-sense oligonucleotide therapeutic targeting RhoBTB2-related epileptic encephalopathy
Title: | O42: Development of an anti-sense oligonucleotide therapeutic targeting RhoBTB2-related epileptic encephalopathy |
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Authors: | Wheeler, Matthew, Bonner, Devon, Alvarez, Raquel, Emami, Sara, Coca, Richard, Willis, Brandon, Mendez, Hector, Patel, Ruchi, Duong, Kate, Arthur, Jennifer, Karakikes, Ioannis, Bernstein, Jonathan, Porter, Brenda, Knowles, Juliet, Lloyd, Kent, LaRocca, Thomas |
Source: | In Genetics in Medicine Open 2024 2 Supplement 1 |
Database: | ScienceDirect |
ISSN: | 29497744 |
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DOI: | 10.1016/j.gimo.2024.101025 |
Published in: | Genetics in Medicine Open |
Language: | English |