Fatal thrombotic microangiopathy case following adeno-associated viral SMN gene therapy

Bibliographic Details
Title: Fatal thrombotic microangiopathy case following adeno-associated viral SMN gene therapy
Authors: Guillou, Julia *, de Pellegars, Alice *, Porcheret, Florence, Frémeaux-Bacchi, Véronique, Allain-Launay, Emma, Debord, Camille, Denis, Manon, Péréon, Yann, Barnérias, Christine, Desguerre, Isabelle *, Roussey, Gwenaëlle *, Mercier, Sandra *
Source: In Blood Advances 26 July 2022 6(14):4266-4270
Database: ScienceDirect
More Details
ISSN:24739529
DOI:10.1182/bloodadvances.2021006419
Published in:Blood Advances
Language:English