Efficacy and safety of odevixibat in patients with Alagille syndrome (ASSERT): a phase 3, double-blind, randomised, placebo-controlled trial

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Title: Efficacy and safety of odevixibat in patients with Alagille syndrome (ASSERT): a phase 3, double-blind, randomised, placebo-controlled trial
Authors: Ovchinsky, Nadia, Aumar, Madeleine, Baker, Alastair *, Baumann, Ulrich, Bufler, Philip, Cananzi, Mara, Czubkowski, Piotr, Durmaz, Özlem, Fischer, Ryan, Indolfi, Giuseppe, Karnsakul, Wikrom W, Lacaille, Florence, Lee, Way S, Maggiore, Giuseppe, Rosenthal, Philip, Ruiz, Mathias, Sokal, Etienne, Sturm, Ekkehard, van der Woerd, Wendy, Verkade, Henkjan J, Wehrman, Andrew, Clemson, Christine, Yu, Qifeng, Ni, Quanhong, Ruvido, Jessica, Manganaro, Susan, Mattsson, Jan P
Source: In The Lancet Gastroenterology & Hepatology July 2024 9(7):632-645
Database: ScienceDirect
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ISSN:24681253
DOI:10.1016/S2468-1253(24)00074-8
Published in:The Lancet Gastroenterology & Hepatology
Language:English