Bibliographic Details
Title: |
DNA-PK inhibition enhances gene editing efficiency in HSPCs for CRISPR-based treatment of X-linked hyper IgM syndrome |
Authors: |
Pugliano, Cole M., Berger, Mason, Ray, Roslyn M., Sapkos, Kai, Wu, Betty, Laird, Aidan, Ye, Yidian, Thomson, Daniel, DeGottardi, M. Quinn, Khan, Iram F., Tatiossian, Kristina, Miles, Brodie A., Aeschimann, Florian, Pasquier, Jerome, Kim, Mihee M., Rawlings, David J. |
Source: |
In Molecular Therapy - Methods & Clinical Development 12 September 2024 32(3) |
Database: |
ScienceDirect |