DNA-PK inhibition enhances gene editing efficiency in HSPCs for CRISPR-based treatment of X-linked hyper IgM syndrome

Bibliographic Details
Title: DNA-PK inhibition enhances gene editing efficiency in HSPCs for CRISPR-based treatment of X-linked hyper IgM syndrome
Authors: Pugliano, Cole M., Berger, Mason, Ray, Roslyn M., Sapkos, Kai, Wu, Betty, Laird, Aidan, Ye, Yidian, Thomson, Daniel, DeGottardi, M. Quinn, Khan, Iram F., Tatiossian, Kristina, Miles, Brodie A., Aeschimann, Florian, Pasquier, Jerome, Kim, Mihee M., Rawlings, David J.
Source: In Molecular Therapy - Methods & Clinical Development 12 September 2024 32(3)
Database: ScienceDirect
More Details
ISSN:23290501
DOI:10.1016/j.omtm.2024.101297
Published in:Molecular Therapy - Methods & Clinical Development
Language:English