An Optimized Lentiviral Vector Efficiently Corrects the Human Sickle Cell Disease Phenotype

Bibliographic Details
Title: An Optimized Lentiviral Vector Efficiently Corrects the Human Sickle Cell Disease Phenotype
Authors: Weber, Leslie, Poletti, Valentina, Magrin, Elisa, Antoniani, Chiara, Martin, Samia, Bayard, Charles, Sadek, Hanem, Felix, Tristan, Meneghini, Vasco, Antoniou, Michael N., El-Nemer, Wassim, Mavilio, Fulvio, Cavazzana, Marina, Andre-Schmutz, Isabelle, Miccio, Annarita
Source: In Molecular Therapy - Methods & Clinical Development 21 September 2018 10:268-280
Database: ScienceDirect
More Details
ISSN:23290501
DOI:10.1016/j.omtm.2018.07.012
Published in:Molecular Therapy - Methods & Clinical Development
Language:English