Non-invasive detection of allele-specific CRISPR-SaCas9-KKH disruption of TOR1A DYT1 allele in a xenograft mouse model

Bibliographic Details
Title:	Non-invasive detection of allele-specific CRISPR-SaCas9-KKH disruption of TOR1A DYT1 allele in a xenograft mouse model
Authors:	Maalouf, Katia E. ^{1, 2, 11}, Frederick, Dawn Madison ^{1, 11}, Sharma, Nutan ², Haidar, Edwina Abou ¹, Xiao, Tianhe ¹, Han, Justin Seungkyu ², Mahamdeh, Mohammed S. ^{3, 4, 5}, Soberman, Roy J. ^{5, 6}, Rufino-Ramos, David ^{7, 8, 9}, Kleinstiver, Benjamin P. ^{7, 8, 9}, Jinnah, Hyder A. ¹⁰, Vaine, Christine A. ², Bragg, D. Cristopher ², Breyne, Koen ^{1, 2, ∗}
Source:	In Molecular Therapy - Nucleic Acids 11 March 2025 36(1)
Database:	ScienceDirect

More Details
ISSN:	21622531
DOI:	10.1016/j.omtn.2025.102466
Published in:	Molecular Therapy - Nucleic Acids
Language:	English