Antisense Oligonucleotide-based Splice Correction for USH2A-associated Retinal Degeneration Caused by a Frequent Deep-intronic Mutation

Bibliographic Details
Title: Antisense Oligonucleotide-based Splice Correction for USH2A-associated Retinal Degeneration Caused by a Frequent Deep-intronic Mutation
Authors: Slijkerman, Radulfus WN **, Vaché, Christel **, Dona, Margo, García-García, Gema, Claustres, Mireille, Hetterschijt, Lisette, Peters, Theo A, Hartel, Bas P, Pennings, Ronald JE, Millan, José M, Aller, Elena, Garanto, Alejandro, Collin, Rob WJ, Kremer, Hannie, Roux, Anne-Françoise *, Van Wijk, Erwin *, *
Source: In Molecular Therapy - Nucleic Acids 2016 5
Database: ScienceDirect
More Details
ISSN:21622531
DOI:10.1038/mtna.2016.89
Published in:Molecular Therapy - Nucleic Acids
Language:English