Bibliographic Details
Title: |
Antisense Oligonucleotide-based Splice Correction for USH2A-associated Retinal Degeneration Caused by a Frequent Deep-intronic Mutation |
Authors: |
Slijkerman, Radulfus WN **, Vaché, Christel **, Dona, Margo, García-García, Gema, Claustres, Mireille, Hetterschijt, Lisette, Peters, Theo A, Hartel, Bas P, Pennings, Ronald JE, Millan, José M, Aller, Elena, Garanto, Alejandro, Collin, Rob WJ, Kremer, Hannie, Roux, Anne-Françoise *, Van Wijk, Erwin *, * |
Source: |
In Molecular Therapy - Nucleic Acids 2016 5 |
Database: |
ScienceDirect |