Efficacy and safety of givosiran for acute hepatic porphyria: Final results of the randomized phase III ENVISION trial
Title: | Efficacy and safety of givosiran for acute hepatic porphyria: Final results of the randomized phase III ENVISION trial |
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Authors: | Kuter, David J., Bonkovsky, Herbert L., Monroy, Susana, Ross, Gayle, Guillén-Navarro, Encarna, Cappellini, Maria Domenica, Minder, Anna-Elisabeth, Hother-Nielsen, Ole, Ventura, Paolo, Jia, Gang, Sweetser, Marianne T., Thapar, Manish |
Source: | In Journal of Hepatology November 2023 79(5):1150-1158 |
Database: | ScienceDirect |
ISSN: | 01688278 |
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DOI: | 10.1016/j.jhep.2023.06.013 |
Published in: | Journal of Hepatology |
Language: | English |