Vector integration and fate in the hemophilia dog liver multiple years after AAV-FVIII gene transfer
Title: | Vector integration and fate in the hemophilia dog liver multiple years after AAV-FVIII gene transfer |
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Authors: | Batty, Paul, Fong, Sylvia, Franco, Matteo, Sihn, Choong-Ryoul, Swystun, Laura L., Afzal, Saira, Harpell, Lorianne, Hurlbut, David, Pender, Abbey, Su, Cheng, Thomsen, Hauke, Wilson, Christopher, Youssar, Loubna, Winterborn, Andrew, Gil-Farina, Irene, Lillicrap, David |
Source: | In Blood 6 June 2024 143(23):2373-2385 |
Database: | ScienceDirect |
ISSN: | 00064971 |
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DOI: | 10.1182/blood.2023022589 |
Published in: | Blood |
Language: | English |