The novel use of the CFTR corrector C17 in muscular dystrophy: pharmacological profile and in vivo efficacy

Bibliographic Details
Title: The novel use of the CFTR corrector C17 in muscular dystrophy: pharmacological profile and in vivo efficacy
Authors: Benetollo, Alberto a, Parrasia, Sofia b, Scano, Martina a, Biasutto, Lucia c, Rossa, Andrea d, Nogara, Leonardo e, Blaauw, Bert a, e, Dalla Barba, Francesco a, Caccin, Paola a, Carotti, Marcello a, Parolin, Alessandro a, Akyürek, Eylem Emek f, Sacchetto, Roberta f, Sandonà, Dorianna a, ⁎
Source: In Biochemical Pharmacology March 2025 233
Database: ScienceDirect
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ISSN:00062952
DOI:10.1016/j.bcp.2025.116779
Published in:Biochemical Pharmacology
Language:English