Therapeutic In Vivo Gene Editing Achieved by a Hypercompact CRISPR‐Cas12f1 System Delivered with All‐in‐One Adeno‐Associated Virus.
Title: | Therapeutic In Vivo Gene Editing Achieved by a Hypercompact CRISPR‐Cas12f1 System Delivered with All‐in‐One Adeno‐Associated Virus. |
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Authors: | Cui, Tongtong1,2, Cai, Bingyu1,2,3, Tian, Yao1,2,3, Liu, Xin1,2,3, Liang, Chen1,2,3, Gao, Qingqin1,2,3, Li, Bojin1,2,3, Ding, Yali1,2,3, Li, Rongqi1,2,3, Zhou, Qi1,2,3,4, Li, Wei1,2,3,4, liwei@ioz.ac.cn, Teng, Fei3, tengfei@ucas.ac.cn |
Source: | Advanced Science; 5/22/2024, Vol. 11 Issue 19, p1-10, 10p |
Database: | Applied Science & Technology Source |
ISSN: | 21983844 |
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DOI: | 10.1002/advs.202308095 |
Published in: | Advanced Science |
Language: | English |