Gene transfer vectors for clinical application

Table of Contents: “…Malech -- Alternative splicing caused by lentiviral intergration in the human genome / Arianna Moiani and Fulvio Mavilio -- Genotoxicity assay for gene therapy vectors in tumor prone Cdkn2a-/-mice / Eugenio Montini and Daniela Cesana -- Lentiviral hematopoietic cell gene therapy for X-linked adrenoleukodystrophy / Nathalie Cartier ... [et al.] -- Retroviral replicating vectors in cancer / Christopher R. …”

Lentiviral Vectors and Gene Therapy by Escors, David, Breckpot, Karine, Arce, Frederick, Kochan, Grazyna, Stephenson, Holly, 1942-

Table of Contents: “….- 6 Human gene therapy with retrovirus and lentivirus vectors -- 6.1 Introduction -- 6.2 Correction of Severe Combined Immunodeficiency-X1 -- 6.3 Correction of X-linked chronic granulomatous disease -- 6.4 Correction of X-linked adrenoleukodystrophy -- 6.5 Correction of b-thalassaemia -- 6.6 Correction of Wiscott-Aldrich syndrome -- 6.7 Conclusions and final considerations.…”
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Pediatric Demyelinating Diseases of the Central Nervous System and Their Mimics A Case-Based Clinical Guide

Table of Contents: “…Neurodegenerative Langerhans Cell Histiocytosis -- 19. X-linked Adrenoleukodystrophy -- 20. Rapid-onset Obesity withHypothalamic dysfunction, Hypoventilation and Autonomic Dysregulation (ROHHAD) -- 21. …”
Available online from ProQuest Ebook Central - Academic Complete: 2017

Pediatric Demyelinating Diseases of the Central Nervous System and Their Mimics : A Case-Based Clinical Guide

Table of Contents: “…Neurodegenerative Langerhans Cell Histiocytosis -- 19. X-linked Adrenoleukodystrophy -- 20. Rapid-onset Obesity with Hypothalamic dysfunction, Hypoventilation and Autonomic Dysregulation (ROHHAD) -- 21. …”
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