Optimizing clinical outcomes: The journey of twins with CRIM-negative infantile-onset Pompe disease on high-dose enzyme replacement therapy and immunomodulation - Fares, Angie H.; Desai, Ankit K.; Case, Laura E.; Sharon, Cassie; Klinepeter, Amy; Kirby, Amelia; Lisi, Matthew T.; Koch, Rebecca L.; Kishnani, Priya S. (Molecular Genetics and Metabolism Reports, 2024)