P786: THROMBOSIS AND MENINGOCOCCAL INFECTION RATES IN PEGCETACOPLAN PATIENTS WITH PAROXYSMAL NOCTURNAL HEMOGLOBINURIA IN THE CLINICAL TRIAL AND POST-MARKETING SETTINGS

Authors: Richard Kelly, Hisakazu Nishimori, Regina Horneff, Peter Hillmen, Jessica Savage, Mohammed Al-Adhami, Stacie Lallier, Gloria Gerber

Source: HemaSphere, Vol 7, p e66610c4 (2023)

Subject Terms: Diseases of the blood and blood-forming organs, RC633-647.5

File Description: electronic resource

Relation: http://journals.lww.com/10.1097/01.HS9.0000970048.66610.c4; https://doaj.org/toc/2572-9241

Access URL: https://doaj.org/article/45057cbce2b34ab3b9c8abb2425525ca

The incidence of hydrocephalus among patients with and without spinal muscular atrophy (SMA): Results from a US electronic health records study

Authors: Emma Viscidi, Nasha Wang, Maneesh Juneja, Ishir Bhan, Claudia Prada, Dayle James, Stacie Lallier, Corinne Makepeace, Karen Laird, Susan Eaton, Anne Dilley, Susan Hall

Source: Orphanet Journal of Rare Diseases, Vol 16, Iss 1, Pp 1-8 (2021)

Subject Terms: Spinal muscular atrophy, Hydrocephalus, Nusinersen, Medicine

File Description: electronic resource

Relation: https://doaj.org/toc/1750-1172

Access URL: https://doaj.org/article/abca1dba3edd41f4afed5f8e28ed15e9