Applying the win ratio method in clinical trials of orphan drugs: an analysis of data from the COMET trial of avalglucosidase alfa in patients with late-onset Pompe disease

Authors: Matthias Boentert, Kenneth I. Berger, Jordi Díaz-Manera, Mazen M. Dimachkie, Alaa Hamed, Lionel Riou França, Nathan Thibault, Pragya Shukla, Jack Ishak, J. Jaime Caro

Source: Orphanet Journal of Rare Diseases, Vol 19, Iss 1, Pp 1-8 (2024)

Subject Terms: Late-onset Pompe disease, Clinical trial, Win ratio, Enzyme replacement therapy, Avalglucosidase alfa, Medicine

File Description: electronic resource

Relation: https://doaj.org/toc/1750-1172

Access URL: https://doaj.org/article/e7b737f3c80f41c2a3616eefc9531926

Novel approach to studying effects of inhalational exposure on lung function in civilians exposed to the World Trade Center disaster

Authors: Yuyan Wang, Kenneth I. Berger, Yian Zhang, Yongzhao Shao, Roberta M. Goldring, Joan Reibman, Mengling Liu

Source: Scientific Reports, Vol 13, Iss 1, Pp 1-12 (2023)

Subject Terms: Medicine, Science

File Description: electronic resource

Relation: https://doaj.org/toc/2045-2322

Access URL: https://doaj.org/article/0b1259677a8e4619b0ba15b658eadc2f

Role of small airway dysfunction in unexplained exertional dyspnoea

Authors: Alexis L. Sharpe, Joan Reibman, Beno W. Oppenheimer, Roberta M. Goldring, Mengling Liu, Yongzhao Shao, Isaac Bohart, Benjamin Kwok, Tatiana Weinstein, Doreen Addrizzo-Harris, Daniel H. Sterman, Kenneth I. Berger

Source: ERJ Open Research, Vol 9, Iss 3 (2023)

Subject Terms: Medicine

File Description: electronic resource

Relation: http://openres.ersjournals.com/content/9/3/00603-2022.full; https://doaj.org/toc/2312-0541

Access URL: https://doaj.org/article/090bb09f13084a8494a53bbdf276cdf1

Electronic cigarettes as a harm reduction strategy among patients with COPD: protocol for an open-label two arm randomized controlled pilot trial

Authors: Elizabeth R. Stevens, Lei Lei, Charles M. Cleland, Mahathi Vojjala, Omar El-Shahawy, Kenneth I. Berger, Thomas R. Kirchner, Scott E. Sherman

Source: Addiction Science & Clinical Practice, Vol 17, Iss 1, Pp 1-11 (2022)

Subject Terms: Medicine (General), R5-920, Social pathology. Social and public welfare. Criminology, HV1-9960

File Description: electronic resource

Relation: https://doaj.org/toc/1940-0640

Access URL: https://doaj.org/article/1a2d8ce3f825411f831c2870959e5072

Development of a standard of care for patients with valosin-containing protein associated multisystem proteinopathy

Authors: Manisha Korb, Allison Peck, Lindsay N. Alfano, Kenneth I. Berger, Meredith K. James, Nupur Ghoshal, Elise Healzer, Claire Henchcliffe, Shaida Khan, Pradeep P. A. Mammen, Sujata Patel, Gerald Pfeffer, Stuart H. Ralston, Bhaskar Roy, William W. Seeley, Andrea Swenson, Tahseen Mozaffar, Conrad Weihl, Virginia Kimonis, the VCP Standards of Care Working Group

Source: Orphanet Journal of Rare Diseases, Vol 17, Iss 1, Pp 1-15 (2022)

Subject Terms: Medicine

File Description: electronic resource

Relation: https://doaj.org/toc/1750-1172

Access URL: https://doaj.org/article/bf65cfbc490c497cb1d7639887c6cbbe

Clinical significance and applications of oscillometry

Authors: David A. Kaminsky, Shannon J. Simpson, Kenneth I. Berger, Peter Calverley, Pedro L. de Melo, Ronald Dandurand, Raffaele L. Dellacà, Claude S. Farah, Ramon Farré, Graham L. Hall, Iulia Ioan, Charles G. Irvin, David W. Kaczka, Gregory G. King, Hajime Kurosawa, Enrico Lombardi, Geoffrey N. Maksym, François Marchal, Ellie Oostveen, Beno W. Oppenheimer, Paul D. Robinson, Maarten van den Berge, Cindy Thamrin

Source: European Respiratory Review, Vol 31, Iss 163 (2022)

Subject Terms: Diseases of the respiratory system, RC705-779

File Description: electronic resource

Relation: http://err.ersjournals.com/content/31/163/210208.full; https://doaj.org/toc/0905-9180; https://doaj.org/toc/1600-0617

Access URL: https://doaj.org/article/0f6fb29b53f245f7b16952e5846ea575

Recommendations for the management of MPS IVA: systematic evidence- and consensus-based guidance

Authors: Mehmet Umut Akyol, Tord D. Alden, Hernan Amartino, Jane Ashworth, Kumar Belani, Kenneth I. Berger, Andrea Borgo, Elizabeth Braunlin, Yoshikatsu Eto, Jeffrey I. Gold, Andrea Jester, Simon A. Jones, Cengiz Karsli, William Mackenzie, Diane Ruschel Marinho, Andrew McFadyen, Jim McGill, John J. Mitchell, Joseph Muenzer, Torayuki Okuyama, Paul J. Orchard, Bob Stevens, Sophie Thomas, Robert Walker, Robert Wynn, Roberto Giugliani, Paul Harmatz, Christian Hendriksz, Maurizio Scarpa, MPS Consensus Programme Steering Committee, MPS Consensus Programme Co-Chairs

Source: Orphanet Journal of Rare Diseases, Vol 14, Iss 1, Pp 1-25 (2019)

Subject Terms: Morquio a syndrome, Mucopolysaccharidosis, MPS IVA, Management guidelines, Elosulfase alfa, VIMIZIM, Medicine

File Description: electronic resource

Relation: http://link.springer.com/article/10.1186/s13023-019-1074-9; https://doaj.org/toc/1750-1172

Access URL: https://doaj.org/article/07788539a8b74b2fa1444bee0867e560

Respiratory impedance measured using impulse oscillometry in a healthy urban population

Authors: Kenneth I. Berger, Margaret Wohlleber, Roberta M. Goldring, Joan Reibman, Mark R. Farfel, Stephen M. Friedman, Beno W. Oppenheimer, Steven D. Stellman, James E. Cone, Yongzhao Shao

Source: ERJ Open Research, Vol 7, Iss 1 (2021)

Subject Terms: Medicine

File Description: electronic resource

Relation: http://openres.ersjournals.com/content/7/1/00560-2020.full; https://doaj.org/toc/2312-0541

Access URL: https://doaj.org/article/5d9bdd9429f941e9999e371bc6732809

Recommendations for the management of MPS VI: systematic evidence- and consensus-based guidance

Authors: Mehmet Umut Akyol, Tord D. Alden, Hernan Amartino, Jane Ashworth, Kumar Belani, Kenneth I. Berger, Andrea Borgo, Elizabeth Braunlin, Yoshikatsu Eto, Jeffrey I. Gold, Andrea Jester, Simon A. Jones, Cengiz Karsli, William Mackenzie, Diane Ruschel Marinho, Andrew McFadyen, Jim McGill, John J. Mitchell, Joseph Muenzer, Torayuki Okuyama, Paul J. Orchard, Bob Stevens, Sophie Thomas, Robert Walker, Robert Wynn, Roberto Giugliani, Paul Harmatz, Christian Hendriksz, Maurizio Scarpa, MPS Consensus Programme Steering Committee, MPS Consensus Programme Co-Chairs

Source: Orphanet Journal of Rare Diseases, Vol 14, Iss 1, Pp 1-21 (2019)

Subject Terms: Maroteaux-Lamy syndrome, Mucopolysaccharidosis, MPS VI, Management guidelines, Galsulfase, Enzyme replacement therapy, Medicine

File Description: electronic resource

Relation: http://link.springer.com/article/10.1186/s13023-019-1080-y; https://doaj.org/toc/1750-1172

Access URL: https://doaj.org/article/4b4cdd98c75840e4a9c116d9983d5417

Small airway function in obese individuals with self-reported asthma

Authors: Beno W. Oppenheimer, Roberta M. Goldring, Israa Soghier, David Smith, Manish Parikh, Kenneth I. Berger

Source: ERJ Open Research, Vol 6, Iss 2 (2020)

Subject Terms: Medicine

File Description: electronic resource

Relation: http://openres.ersjournals.com/content/6/2/00371-2019.full; https://doaj.org/toc/2312-0541

Access URL: https://doaj.org/article/604d6c713894410b9b3d9f6188d7c26a

Distal airway dysfunction identifies pulmonary inflammation in asymptomatic smokers

Authors: Kenneth I. Berger, Deepak R. Pradhan, Roberta M. Goldring, Beno W. Oppenheimer, William N. Rom, Leopoldo N. Segal

Source: ERJ Open Research, Vol 2, Iss 4 (2016)

Subject Terms: Medicine

File Description: electronic resource

Relation: http://openres.ersjournals.com/content/2/4/00066-2016.full; https://doaj.org/toc/2312-0541

Access URL: https://doaj.org/article/c0a537bfe73a4b7d920f83e8d0c4057c

Oscillometry complements spirometry in evaluation of subjects following toxic inhalation

Authors: Kenneth I. Berger, Meredith Turetz, Mengling Liu, Yongzhao Shao, Angeliki Kazeros, Sam Parsia, Caralee Caplan-Shaw, Stephen M. Friedman, Carey B. Maslow, Michael Marmor, Roberta M. Goldring, Joan Reibman

Source: ERJ Open Research, Vol 1, Iss 2 (2015)

Subject Terms: Medicine

File Description: electronic resource

Relation: http://openres.ersjournals.com/content/1/2/00043-2015.full; https://doaj.org/toc/2312-0541

Access URL: https://doaj.org/article/52a816651c944c5588fef8640dc0fbdf

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Pulmonary Vascular Congestion: A Mechanism for Distal Lung Unit Dysfunction in Obesity.

Authors: Beno W Oppenheimer, Kenneth I Berger, Saleem Ali, Leopoldo N Segal, Robert Donnino, Stuart Katz, Manish Parikh, Roberta M Goldring

Source: PLoS ONE, Vol 11, Iss 4, p e0152769 (2016)

Subject Terms: Medicine, Science

File Description: electronic resource

Relation: http://europepmc.org/articles/PMC4817979?pdf=render; https://doaj.org/toc/1932-6203

Access URL: https://doaj.org/article/85b81d369a7f468d8acc9c03de3bb6bb

Airway dysfunction in obesity: response to voluntary restoration of end expiratory lung volume.

Authors: Beno W Oppenheimer, Kenneth I Berger, Leopoldo N Segal, Alexandra Stabile, Katherine D Coles, Manish Parikh, Roberta M Goldring

Source: PLoS ONE, Vol 9, Iss 2, p e88015 (2014)

Subject Terms: Medicine, Science

File Description: electronic resource

Relation: http://europepmc.org/articles/PMC3913722?pdf=render; https://doaj.org/toc/1932-6203

Access URL: https://doaj.org/article/c0a79360986e4f519281b301208a6ec7