Treatment of infantile-onset Pompe disease in a rat model with muscle-directed AAV gene therapy

Authors: Sergio Muñoz, Joan Bertolin, Veronica Jimenez, Maria Luisa Jaén, Miquel Garcia, Anna Pujol, Laia Vilà, Victor Sacristan, Elena Barbon, Giuseppe Ronzitti, Jihad El Andari, Warut Tulalamba, Quang Hong Pham, Jesus Ruberte, Thierry VandenDriessche, Marinee K. Chuah, Dirk Grimm, Federico Mingozzi, Fatima Bosch

Source: Molecular Metabolism, Vol 81, Iss , Pp 101899- (2024)

Subject Terms: Glycogen metabolism, Myopathies, Pompe disease, Rat model, Gene therapy, AAV, Internal medicine, RC31-1245

File Description: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2212877824000309; https://doaj.org/toc/2212-8778

Access URL: https://doaj.org/article/51f4889c5f3c445fbc764529166584d8

High throughput screening of novel AAV capsids identifies variants for transduction of adult NSCs within the subventricular zone

Authors: Lukas P.M. Kremer, Santiago Cerrizuela, Sascha Dehler, Thomas Stiehl, Jonas Weinmann, Heike Abendroth, Susanne Kleber, Alexander Laure, Jihad El Andari, Simon Anders, Anna Marciniak-Czochra, Dirk Grimm, Ana Martin-Villalba

Source: Molecular Therapy: Methods & Clinical Development, Vol 23, Iss , Pp 33-50 (2021)

Subject Terms: neural stem cells, ventricular-subventricular zone, v-SVZ, adeno-associated virus, AAV, gene therapy, Genetics, QH426-470, Cytology, QH573-671

File Description: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050121001182; https://doaj.org/toc/2329-0501

Access URL: https://doaj.org/article/20c78c1f028844548046b6a391c1e845

Identification of a myotropic AAV by massively parallel in vivo evaluation of barcoded capsid variants

Authors: Jonas Weinmann, Sabrina Weis, Josefine Sippel, Warut Tulalamba, Anca Remes, Jihad El Andari, Anne-Kathrin Herrmann, Quang H. Pham, Christopher Borowski, Susanne Hille, Tanja Schönberger, Norbert Frey, Martin Lenter, Thierry VandenDriessche, Oliver J. Müller, Marinee K. Chuah, Thorsten Lamla, Dirk Grimm

Source: Nature Communications, Vol 11, Iss 1, Pp 1-12 (2020)

Subject Terms: Science

File Description: electronic resource

Relation: https://doaj.org/toc/2041-1723

Access URL: https://doaj.org/article/fcda7a44d2044540880d0f383706efd9

Molecular Signature of Astrocytes for Gene Delivery by the Synthetic Adeno‐Associated Viral Vector rAAV9P1

Authors: Amelie Bauer, Matteo Puglisi, Dennis Nagl, Joel A Schick, Thomas Werner, Andreas Klingl, Jihad El Andari, Veit Hornung, Horst Kessler, Magdalena Götz, Dirk Grimm, Ruth Brack‐Werner

Source: Advanced Science, Vol 9, Iss 16, Pp n/a-n/a (2022)

Subject Terms: AAV, Adeno‐associated virus, astrocytes, integrins, receptor profile, vectors, Science

File Description: electronic resource

Relation: https://doaj.org/toc/2198-3844

Access URL: https://doaj.org/article/5af49d6d446a4dbebfe51b5777d11b6c

Novel Chimeric Gene Therapy Vectors Based on Adeno-Associated Virus and Four Different Mammalian Bocaviruses

Authors: Julia Fakhiri, Marc A. Schneider, Jens Puschhof, Megan Stanifer, Verena Schildgen, Stefan Holderbach, Yannik Voss, Jihad El Andari, Oliver Schildgen, Steeve Boulant, Michael Meister, Hans Clevers, Ziying Yan, Jianming Qiu, Dirk Grimm

Source: Molecular Therapy: Methods & Clinical Development, Vol 12, Iss , Pp 202-222 (2019)

Subject Terms: Genetics, QH426-470, Cytology, QH573-671

File Description: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050119300063; https://doaj.org/toc/2329-0501

Access URL: https://doaj.org/article/7fbe1a7cee86481baac8bf16199ef869

Induction of Hepatitis E Virus Anti-ORF3 Antibodies from Systemic Administration of a Muscle-Specific Adeno-Associated Virus (AAV) Vector

Authors: Lars Maurer, Jihad El Andari, Kleopatra Rapti, Laura Spreyer, Eike Steinmann, Dirk Grimm, Viet Loan Dao Thi

Source: Viruses, Vol 14, Iss 2, p 266 (2022)

Subject Terms: adeno-associated virus, AAV, hepatitis E virus, HEV, vector-based vaccine, neutralisation, Microbiology, QR1-502

File Description: electronic resource

Relation: https://www.mdpi.com/1999-4915/14/2/266; https://doaj.org/toc/1999-4915

Access URL: https://doaj.org/article/59f135ac156247f2869a8a5148203a1d

Bacillus subtilis Bactofilins Are Essential for Flagellar Hook- and Filament Assembly and Dynamically Localize into Structures of Less than 100 nm Diameter underneath the Cell Membrane.

Authors: Jihad El Andari, Florian Altegoer, Gert Bange, Peter L Graumann

Source: PLoS ONE, Vol 10, Iss 10, p e0141546 (2015)

Subject Terms: Medicine, Science

File Description: electronic resource

Relation: http://europepmc.org/articles/PMC4627819?pdf=render; https://doaj.org/toc/1932-6203

Access URL: https://doaj.org/article/3ba899d1951f44509fd87dc2b0510a56