Rational design of base, sugar and backbone modifications improves ADAR-mediated RNA editing.

Authors: Lu, Genliang, Shivalila, Chikdu, Monian, Prashant, Yu, Hui, Harding, Ian, Briem, Stearne, Byrne, Michael, Faraone, Alyse, Friend, Stephen, Huth, Olivia, Iwamoto, Naoki, Kawamoto, Tomomi, Kumarasamy, Jayakanthan, Lamattina, Anthony, Longo, Kenneth, McCarthy, Leah, McGlynn, Andrew, Molski, Allison, Pan, Qianli, Pu, Tom

Source: Nucleic Acids Research; 9/23/2024, Vol. 52 Issue 17, p10068-10084, 17p

FRI-151 RNA editing for the treatment of Alpha-1 antitrypsin deficiency

Authors: Monian, Prashant, Lu, Genliang, Shivalila, Chikdu, Bowman, Keith, Bylsma, Marissa, Byrne, Michael, Cannon, Megan, Desai, Jigar, Faraone, Alyse, Favaloro, Frank, Ghosh, Anamitra, Godfrey, Jack, Hernandez, Nidia, Huth, Olivia, Iwamoto, Naoki, Kawamoto, Tomomi, Kumarasamy, Jayakanthan, Kandasamy, Pachamuthu, Lamattina, Anthony, Lindsey, Amber, Liu, Fangjun, Looby, Richard, Luu, Khoa, Metterville, Jake, Paik, Ik-Hyeon, Pan, Qianli, Purcell-Estabrook, Erin, Rheinhardt, Jeanette, Shimizu, Mamoru, Singh, Kuldeep, Standley, Stephany, Thomas, Carina, Tripathi, Snehlata, Yang, Hailin, Yordanoff, Ryan, Yin, Benny, Yu, Hui, Caracta, Cynthia, Narayanan, Padma, Giangrande, Paloma, Vargeese, Chandra

Source: In Journal of Hepatology June 2024 80 Supplement 1:S692-S693