Hematopoietic cell transplant compared with standard care in adolescents and young adults with sickle cell disease

Authors: Walters, Mark C. ¹, Eapen, Mary ², Liu, Yiwen ³, El Rassi, Fuad ⁴, Waller, Edmund K. ⁴, Levine, John E. ⁵, Strouse, John J. ⁶, Antin, Joseph H. ⁷, Parikh, Suhag H. ⁸, Bakshi, Nitya ^{8, 9}, Dampier, Carlton ⁸, Jaroscak, Jennifer J. ¹⁰, Bergmann, Shayla ¹⁰, Wong, Trisha ¹¹, Kota, Vamsi ¹², Pace, Betty ¹³, Lekakis, Lazaros J. ¹⁴, Lulla, Premal ¹⁵, Nickel, Robert S. ¹⁶, Kasow, Kimberly A. ¹⁷, Popat, Uday ¹⁸, Smith, Wally ¹⁹, Yu, Lolie ²⁰, DiFronzo, Nancy ²¹, Geller, Nancy ²², Kamani, Naynesh ²³, Klings, Elizabeth S. ²⁴, Hassell, Kathryn ²⁵, Mendizabal, Adam ²⁶, Sullivan, Keith ²⁷, Neuberg, Donna ³, Krishnamurti, Lakshmanan ^{8, 9, ∗}

Source: In Blood Advances 11 March 2025 9(5):955-965

Secondary Neoplasms After Hematopoietic Cell Transplant for Sickle Cell Disease

Authors: Eapen, Mary, Brazauskas, Ruta, Williams, David A., Walters, Mark C., St Martin, Andrew, Jacobs, Benjamin L., Antin, Joseph H., Bona, Kira, Chaudhury, Sonali, Coleman-Cowger, Victoria H., DiFronzo, Nancy L., Esrick, Erica B., Field, Joshua J., Fitzhugh, Courtney D., Kanter, Julie, Kapoor, Neena, Kohn, Donald B., Krishnamurti, Lakshmanan, London, Wendy B., Pulsipher, Michael A., Talib, Sohel, Thompson, Alexis A., Waller, Edmund K., Wun, Ted, Horowitz, Mary M.

Source: Journal of clinical oncology. 41(12):2227-2237

Availability: http://explore.bl.uk/primo_library/libweb/action/display.do?tabs=detailsTab&gathStatTab=true&ct=display&fn=search&doc=ETOCvdc_100189911416.0x000001&indx=1&recIds=ETOCvdc_100189911416.0x000001

Bringing Patient and Caregivers Voices to the Clinical Trial Chorus: A Report From the BMT CTN Patient and Caregiver Advocacy Task Force

Authors: Vasu, Sumithira, Holtan, Shernan G., Shimamura, Akiko, Burnworth, Todd, Whisenton, Shauna, Adams, Sanderson, Nuechterlein, Brandon, Mortier, Nicole, Foster, Jackie, DiFronzo, Nancy, Horowitz, Mary, Rizzo, Doug, Foley, Amy

Source: Transplantation and Cellular Therapy. 29(1):5-9

Availability: http://explore.bl.uk/primo_library/libweb/action/display.do?tabs=detailsTab&gathStatTab=true&ct=display&fn=search&doc=ETOCvdc_100180472408.0x000001&indx=1&recIds=ETOCvdc_100180472408.0x000001

Utility of targeted gene sequencing to differentiate myeloid malignancies from other cytopenic conditions

Authors: DeZern, Amy E., Goll, Johannes B., Lindsley, R. Coleman, Bejar, Rafael, Wilson, Steffanie H., Hebert, Donnie, Deeg, Joachim, Zhang, Ling, Gore, Steven, Al Baghdadi, Tareq, Maciejewski, Jaroslaw, Liu, Jane, Padron, Eric, Komrojki, Rami, Saber, Wael, Abel, Gregory, Kroft, Steven H., Harrington, Alexandra, Grimes, Tyler, Reed, Harrison, Fulton, Robert S., DiFronzo, Nancy L., Gillis, Nancy, Sekeres, Mikkael A., Walter, Matthew J.

Source: In Blood Advances 25 July 2023 7(14):3749-3759

Priorities for Improving Outcomes for Nonmalignant Blood Diseases: A Report from the Blood and Marrow Transplant Clinical Trials Network

Authors: Levine, John E., Antin, Joseph H., Allen, Carl E., Burroughs, Lauri M., Cooke, Kenneth R., Devine, Steven, Heslop, Helen, Nakamura, Ryotaro, Talano, Julie An, Yanik, Gregory, DiFronzo, Nancy

Source: Biology of blood and marrow transplantation. 26(5):e94-e100

Availability: http://explore.bl.uk/primo_library/libweb/action/display.do?tabs=detailsTab&gathStatTab=true&ct=display&fn=search&doc=ETOCvdc_100121458775.0x000001&indx=1&recIds=ETOCvdc_100121458775.0x000001

Correlation between peripheral blood and bone marrow mutations among patients with MDS from the National MDS Study

Authors: DeZern, Amy E., Goll, Johannes B., Jensen, Travis L., Nonavinkere Srivatsan, Sridhar, Gillis, Nancy K., Abel, Gregory A., Padron, Eric, Deeg, H. Joachim, Al Baghdadi, Tareq, Liu, Jane Jijun, Komrokji, Rami S., Gore, Steven D., Saber, Wael, Bejar, Rafael, Walter, Matthew J., Lindsley, R. Coleman, Sherman, Seth, DiFronzo, Nancy, Sekeres, Mikkael A.

Source: In Blood Neoplasia September 2024 1(3)

The National MDS Natural History Study: design of an integrated data and sample biorepository to promote research studies in myelodysplastic syndromes

Authors: Sekeres, Mikkael A., Gore, Steven D., Stablein, Donald M., DiFronzo, Nancy, Abel, Gregory A., DeZern, Amy E., Troy, Jesse D., Rollison, Dana E., Thomas, John W., Waclawiw, Myron A., Liu, Jane Jijun, Al Baghdadi, Tareq, Walter, Matthew J., Bejar, Rafael, Gorak, Edward J., Starczynowski, Daniel T., Foran, James M., Cerhan, James R., Moscinski, Lynn C., Komrokji, Rami S., Deeg, H. Joachim, Epling-Burnette, Pearlie K.

Source: Leukemia & lymphoma. 60(13):3161-3171

Availability: http://explore.bl.uk/primo_library/libweb/action/display.do?tabs=detailsTab&gathStatTab=true&ct=display&fn=search&doc=ETOCvdc_100097991352.0x000001&indx=1&recIds=ETOCvdc_100097991352.0x000001

A trial of unrelated donor marrow transplantation for children with severe sickle cell disease

Authors: Shenoy, Shalini, Eapen, Mary, Panepinto, Julie A., Logan, Brent R., Wu, Juan, Abraham, Allistair, Brochstein, Joel, Chaudhury, Sonali, Godder, Kamar, Haight, Ann E., Kasow, Kimberly A., Leung, Kathryn, Andreansky, Martin, Bhatia, Monica, Dalal, Jignesh, Haines, Hilary, Jaroscak, Jennifer, Lazarus, Hillard M., Levine, John E., Krishnamurti, Lakshmanan, Margolis, David, Megason, Gail C., Yu, Lolie C., Pulsipher, Michael A., Gersten, Iris, DiFronzo, Nancy, Horowitz, Mary M., Walters, Mark C., Kamani, Naynesh

Source: In Blood 24 November 2016 128(21):2561-2567

Humoral Immunogenicity of Sars-Cov-2 Vaccination in the First Year after Hematopoietic Cell Transplant or Chimeric Antigen Receptor T Cell Therapy: A CIBMTR and BMT CTN Study

Authors: Riches, Marcie L., Hill, Joshua A., Martens, Michael, Auletta, Jeffery James, Baluch, Aliyah, Bhavsar, Kavita, Brown, Janice (Wes), Dhodapkar, Madhav Vishnu, DiFronzo, Nancy, Howard, Alan, Ibrahim, Uroosa, Nakamura, Ryotaro, Peyton, Kristin, Shahid, Zainab, Sharon, Elad, Spahn, Ashley, Toor, Amir A., Waldvogel, Stephanie, Westervelt, Peter, Young, Jo-Anne H., Perales, Miguel-Angel, Horowitz, Mary M.

Source: Transplantation and Cellular Therapy. 28(S):S372-S373

Availability: http://explore.bl.uk/primo_library/libweb/action/display.do?tabs=detailsTab&gathStatTab=true&ct=display&fn=search&doc=ETOCvdc_100157889241.0x000001&indx=1&recIds=ETOCvdc_100157889241.0x000001

Randomized, Double-Blind, Placebo-Controlled Trial of Soluble Tumor Necrosis Factor Receptor: Enbrel (Etanercept) for the Treatment of Idiopathic Pneumonia Syndrome after Allogeneic Stem Cell Transplantation: Blood and Marrow Transplant Clinical Trials Network Protocol

Authors: Yanik, Gregory A., Horowitz, Mary M., Weisdorf, Daniel J., Logan, Brent R., Ho, Vincent T., Soiffer, Robert J., Carter, Shelly L., Wu, Juan, Wingard, John R., Difronzo, Nancy L., Ferrara, James L., Giralt, Sergio, Madtes, David K., Drexler, Rebecca, White, Eric S., Cooke, Kenneth R.

Source: In Biology of Blood and Marrow Transplantation June 2014 20(6):858-864

Optimization of Therapy for Severe Aplastic Anemia Based on Clinical, Biologic, and Treatment Response Parameters: Conclusions of an International Working Group on Severe Aplastic Anemia Convened by the Blood and Marrow Transplant Clinical Trials Network, March 2010

Authors: Pulsipher, Michael A., Young, Neal S., Tolar, Jakub, Risitano, Antonio M., Deeg, H. Joachim, Anderlini, Paolo, Calado, Rodrigo, Kojima, Seiji, Eapen, Mary, Harris, Richard, Scheinberg, Phillip, Savage, Sharon, Maciejewski, Jaroslaw P., Tiu, Ramon V., DiFronzo, Nancy, Horowitz, Mary M., Antin, Joseph H.

Source: In Biology of Blood and Marrow Transplantation 2011 17(3):291-299

Donor Search and Selection Strategy to Facilitate Comparable Transplant Rates across Donor Search Prognosis Groups: A Report from the BMT CTN 1702 Trial

Authors: Pidala, Joseph A., Logan, Brent, He, Naya, Lee, Stephanie J, Ciurea, Stefan O., Devine, Steven M., Shaw, Bronwen E., Vogel, Jenny, Erickson, Connor, Bashey, Asad, Doyle, Jerry, DiFronzo, Nancy, Farhadfar, Nosha, Grunwald, Mike R., Hayes-Lattin, Brandon, Henderson, Lori, Hogan, William J., Horowitz, Mary M., Leifer, Eric, Symons, Heather, Pusic, Dr. Iskra, Srour, Samer A., Arai, Sally, Juckett, Mark, Howard, Dianna S., Uberti, Joseph, Hill, LaQuisa Chimere, Vasu, Sumithira, Dehn, Jason

Source: In Transplantation and Cellular Therapy February 2024 30(2) Supplement:S20-S20

Etanercept, mycophenolate, denileukin, or pentostatin plus corticosteroids for acute graft-versus-host disease: a randomized phase 2 trial from the Blood and Marrow Transplant Clinical Trials Network

Authors: Alousi, Amin M., Weisdorf, Daniel J., Logan, Brent R., Bolaños-Meade, Javier, Carter, Shelly, DiFronzo, Nancy, Pasquini, Marcelo, Goldstein, Steven C., Ho, Vincent T., Hayes-Lattin, Brandon, Wingard, John R., Horowitz, Mary M., Levine, John E.

Source: In Blood 16 July 2009 114(3):511-517

Correlation between Peripheral Blood and Bone Marrow Somatic Mutations Among Patients with Suspected or Established Myelodysplastic Syndromes from the National MDS Study

Authors: DeZern, Amy E., Goll, Johannes, Jensen, Travis L, Srivatsan, Sridhar N, Gillis, Nancy K, Abel, Gregory A, Padron, Eric, Deeg, H. Joachim, Al Baghdadi, Tareq, Liu, Jane Lijun, Komrokji, Rami S., Gore, Steven D., Saber, Wael, Bejar, Rafael, Walter, Matthew J., Sherman, Seth, DiFronzo, Nancy, Sekeres, Mikkael A.

Source: In Blood 2 November 2023 142 Supplement 1:1860-1860

Patient-Reported Outcomes of BMT CTN 1703: A Randomized Phase III Study for Gvhd Prophylaxis - a Quality of Life Evaluation

Authors: Holtan, Shernan G., Martens, Michael J, Al Malki, Monzr M., Efebera, Yvonne, Kitko, Carrie L., Reshef, Ran, Rezvani, Andrew R., Shaffer, Brian C., Solh, Melhem M., Yao, Janny M., Runaas, Lyndsey, Elmariah, Hany, Larkin, Karilyn T., El Jurdi, Najla H, Gooptu, Mahasweta, Loren, Alison W, Hall, Aric C., Alousi, Amin, Jamy, Omer, Clark, William, Kean, Leslie, Bhatt, Ami S., Perales, Miguel-Angel, Applegate, Kristy, WU, Juan, Liefer, Eric, DiFronzo, Nancy, Jones, Richard J., Horowitz, Mary M., Mattila, Deborah, Hamadani, Mehdi, Bolanos-Meade, Javier

Source: In Blood 2 November 2023 142 Supplement 1:897-897

Post-Transplant Cyclophosphamide, Tacrolimus, and Mycophenolate Mofetil As the New Standard for Graft-Versus-Host Disease (GVHD) Prophylaxis in Reduced Intensity Conditioning: Results from Phase III BMT CTN 1703

Authors: Holtan, Shernan G, Hamadani, Mehdi, WU, Juan ^∗, AL Malki, Monzr M., Runaas, Lyndsey ^∗, Elmariah, Hany, Rezvani, Andrew R., Gooptu, Mahasweta, Larkin, Karilyn T., Shaffer, Brian C., El Jurdi, Najla H, Loren, Alison W., Solh, Melhem, Hall, Aric C. ^∗, Alousi, Amin M, Jamy, Omer H, Perales, Miguel-Angel, Yao, Janny M. ^∗, Applegate, Kristy ^∗, Bhatt, Ami S., Kean, Leslie S., Efebera, Yvonne A., Kitko, Carrie Lynn, Reshef, Ran, Clark, William ^∗, DiFronzo, Nancy L. ^∗, Henderson, Lori ^∗, Jones, Richard J., Liefer, Eric ^∗, Martens, Michael J ^∗, Horowitz, Mary M., Bolanos-Meade, Javier

Source: In Blood 6 December 2022 140 Supplement 2

Hematopoietic Cell Transplantation (HCT) Predictions for the Year 2023

Authors: Farhadfar, Nosha, Burns, Linda J., Mupfudze, Tatenda, Shaw, Bronwen E., Bollard, Catherine M., Devine, Steven M., DiFronzo, Nancy, Horowitz, Mary M., Jones, Richard J., Murthy, Hemant, Wingard, John R., Lee, Stephanie

Source: Biology of blood and marrow transplantation. 26(S):S201-S201

Availability: http://explore.bl.uk/primo_library/libweb/action/display.do?tabs=detailsTab&gathStatTab=true&ct=display&fn=search&doc=ETOCvdc_100100239344.0x000001&indx=1&recIds=ETOCvdc_100100239344.0x000001

475 - Humoral Immunogenicity of Sars-Cov-2 Vaccination in the First Year after Hematopoietic Cell Transplant or Chimeric Antigen Receptor T Cell Therapy: A CIBMTR and BMT CTN Study

Authors: Riches, Marcie L., Hill, Joshua A., Martens, Michael, Auletta, Jeffery James, Baluch, Aliyah, Bhavsar, Kavita, Brown, Janice (Wes), Dhodapkar, Madhav Vishnu, DiFronzo, Nancy, Howard, Alan, Ibrahim, Uroosa, Nakamura, Ryotaro, Peyton, Kristin, Shahid, Zainab, Sharon, Elad, Spahn, Ashley, Toor, Amir A., Waldvogel, Stephanie, Westervelt, Peter, Young, Jo-Anne H., Perales, Miguel-Angel, Horowitz, Mary M.

Source: In Transplantation and Cellular Therapy March 2022 28(3) Supplement:S372-S373

COVID-19 Outcomes Among Participants in the NHLBI Myelodysplastic Syndromes (MDS) Natural History Study

Authors: Padron, Eric, Hebert, Donnie, Gore, Steven D., Gillis, Nancy, Komrokji, Rami S., Saber, Wael, Al Baghdadi, Tareq, Liu, Jane Jijun, Gorak, Edward J., Lee, Cecilia, Borchert, Christine, Wilson, Steffanie H., Thompson, Jason, Walker, Mary Ellen, DiFronzo, Nancy L., DeZern, Amy E., Sekeres, Mikkael A.

Source: In Blood 23 November 2021 138 Supplement 1:2611-2611

Pulmonary Complications of Pediatric Hematopoietic Cell Transplantation. A National Institutes of Health Workshop Summary.

Authors: Tamburro, Robert F., Cooke, Kenneth R., Davies, Stella M., Goldfarb, Samuel, Hagood, James S., Srinivasan, Ashok, Steiner, Marie E., Stokes, Dennis, DiFronzo, Nancy, El-Kassar, Nahed, Shelburne, Nonniekaye, Natarajan, Aruna, Pulmonary Complications of Pediatric Hematopoietic Stem Cell Transplantation Workshop Participants

Source: Annals of the American Thoracic Society; Mar2021, Vol. 18 Issue 3, p381-394, 14p

Subject Terms: HEMATOPOIETIC growth factors, GRAFT versus host disease, LUNG disease treatment, ADULT respiratory distress syndrome treatment, PEDIATRICS