Safety and efficacy of a fitusiran antithrombin-based dose regimen in people with hemophilia A or B: the ATLAS-OLE study

Authors: Khoo, Teh-Liane, Dunkley, Scott, P'ng, Stephanie, Pepperell, Dominic, Lam, Stephanie, Steinepreis, Elizabeth, Malherbe, Jacques, Kendrick, Tulene, Lombard, Marcus, Tran, Huyen, Zhao, Jessie, Stevens, Hannah, Dix, Caroline, McFadyen, James, St-Louis, Jean, Kassis, Jeannine, Rivard, Georges, Sun, Jing, Li, Xiaofang, Li, Huiping, Ye, Jieyu, Zhou, Xuan, Du, Dong, Wang, Xuefeng, Dai, Jing, Ding, Quilan, Wu, Wenman, Lu, Yiyi, Wu, Runhui, Liu, Guoqing, Yao, Wanru, Wang, Yan, Wei, Yunyun, Xu, Weiqun, Du, Yu, Xu, Liyao, Wang, Di, Liao, Chan, Zhang, Hongwei, Yu, Ziqiang, Tian, Hong, Wang, Haibo, Yin, Jie, Zhu, Tienan, Cai, Huacong, Xiao, Juan, Wang, Shujie, Liu, Shufen, Shen, Kaini, Chen, Yun, Chang, Yali, Sang, Tan, Zhao, Jun, Zhou, Yawei, Zhai, Liya, Qiu, Xiadong, He, Yulei, Li, Hui, Xia, Yi, Zhou, Min, Gao, Feng, Feng, Shipin, Luo, Xiaoli, Li, Dan, Cui, Zhongguang, Zhao, Chunzhu, Xu, Hong, Sun, Lingjie, Shi, Xue, Zeng, Xiaojing, Qi, Lu, Cao, Shuyun, Zhou, Zeping, Zhang, Fuhou, Yin, Lingmei, Mu, Hongli, Bi, Hui, Li, Zhengchao, Miu, Yaping, Xi, Yaming, Jia, Mingfeng, Zhao, Long, Zhao, Xielan, Li, Yaochun, Peng, Jie, Chang, Chia-Yau, Liu, Yen-Lin, Shen, Ming-Ching, Huang, Cheng-Wei, Wang, Shih-Chung, Lin, Hsuan-Yu, Lin, Ching-Yeh, Chou, Sheng-Chieh, Chuang, Ming-Kai, Hsu, Szu-Chun, Wang, Jiaan-Der, Shih, Ming-Yang, Hsiao, Liang-Tsai, Hung, Giun-Yi, Yen, Hsiu-Ju, Ko, Po-Shen, Chang, Hung, Chen, Shih-Hsaing, Weng, Te-Fu, Chao, Yu-Hua, Zeng, Sherig-Wei, Kampmann, Peter, Funding, Eva, Dargaud, Yesim, Negrier, Claude, Desag, Stéphanie, Frenzel, Laurent, Fouquet, Guillemette, Bally, Cécile, Klamroth, Robert, Orlovic, Ana-Marija, Pfrepper, Christian, Metze, Michael, Chakaroun, Rima, Weise, Maria, Nemes, László, Ronatas, Agnes, Ross, Cecil, Anandram, Seetharam, Bharadwaj, Vandana, Salvi, Sonali, Lohande, Sunil, Srivastava, Alok, Abraham, Aby, Aboobacker, Fouzia, Verma, Shailendra, Datta, Gaurav, Rangarajan, Savita, Bansal, Shweta, Apte, Shashikant, Subramanian, Kannan, Nolan, Beatrice, Ahmed, Saad, O’Connell, Niamh, O’Donnell, James, Ryan, Kevin, Lavin, Michelle, Kenet, Gili, Cohen, Omri, Misgav, Mudi, Barg, Assaf, Mendelovich, Sarina Levy, Peyvandi, Flora, Gualtierotti, Roberta, Zanon, Ezio, Spiezia, Luca, Simion, Chiara, Matsushita, Tadashi, Okamoto, Shuichi, Suzuki, Nobuaki, Kanematsu, Takeshi, Suzuki, Naruko, Kawaguchi, Yuka, Higasa, Satoshi, Tokugawa, Tazuko, Sawada, Akihiro, Shirayama, Rie, Kawamura, Masaru, Asai, Hiroshi, Oshida, Koichi, Sato, Tetsuji, Ito, Takuma, Koh, Katsuyoshi, Mizushima, Yoshitaka, Ishikawa, Takahiro, Kubota, Hirohito, Kaneko, Ryota, Irikura, Tomoya, Honda, Mamoru, Taira, Katsuaki, Arakawa, Yuki, Mori, Makiko, Fukoka, Kohei, Oshima, Koichi, Mitani, Yuichi, Ogawa, Yoshiaki, Ando, Kiyoshi, Suzuki, Rikio, Hara, Ryujiro, Aoyama, Yasuyuki, Toyosaki, Masako, Ogiya, Daisuke, Machida, Shinichiro, Kawada, Hiroshi, Shirasugi, Yukari, Onizuka, Makoto, Omachi, Ken, Amano, Kagehiro, Yamaguchi, Tomoko, Kinai, Ei, Hagiwara, Takeshi, Yotsumoto, Mihoko, Sekiya, Ryoko, Bingo, Masato, Chikasawa, Yushi, Ichiki, Akito, Kamikubo, Yoshiko, Miyashita, Ryui, Muramatsu, Takashi, Shin, Ho-Jin, Kim, DoYoung, You, Chur-Woo, Kim, Ju Young, Hahn, Seung Min, Lyu, Chuhl Joo, Han, Jung Woo, Park, Young Shil, Cho, Ja Hyang, Shariq, Azizan, Lim, Soo Min, Wong, Lily, Chang Choo, Heng, Wilfred, Gilbert, Ahmad Zakhi, Mohd Tarmizi, Lim, Yin Man, Raghunathan, Khaiteri, Sathar, Jameela, Nasution, Syazarin Fidhora, Yap, Yee Yee, Selvaratnam, Veena, Malan, Daniel, Punt, Zelda Erika, Antmen, Ali Bulent, Sasmaz, Ilgen, Aygunes, Utku, Kavakli, Kaan, Karadas, Nihal, Karapinar, Deniz, Kupesiz, Alphan, Erkan, Mine, Tayfun, Kupesiz Funda, Guler, Elif, Zulfikar, Bulent, Koc, Basak, Okan, Vahap, Haydaroglu, Sahin Handan, Albayrak, Canan, Kartal, Ibrahim, Yilmaz, Ebru, Karakukcu, Musa, Unal, Ekrem, Ozcan, Alper, Sahin, Fahri, Tuzun, Betul, Saydam, Guray, Averianov, Ievgenii, Kovtunenko, Oksana, Stasyshyn, Oleksandra, Semerak, Maksym, Tushnytskyy, Orest, Vilchevska, Kateryna, Bakhchyvandzhy, Iryna, Romanyuk, Nataliya, Nikulin, Stanislav, Kobets, Alina, Alamelu MRCPCH, Jayanthi, Babiker, Samah, Bagot, Catherine, Rodgers, James Tyan, Boggio, Lisa, Simpson, Mindy, Cockrell, Erin, DeBerry, Candance, Obzut, Dana, Fargo, John, Hord, Jeffrey, Savelli, Stephanie, Lasky, Joseph, Buitrago, Jennifer, Alhushki, Waseem, Gauger, Cynthia, Klawinski, Darren, Sandler, Eric, Bradfield, Scott, Pitel, Paul, Joyce, Michael, Katzenstein, Howard, Bansal, Manisha, Bechtel, Allison, Knoll, Christine, Gomez, Esteban, White, Shanna, Shah, Sanjay, Gendreau, Joanna, Wagner, Lori, Quarmyne, Maa-Ohui, Bornikova, Larissa, Cleary CNP, Colleen, Hodges, Pamela G., Mossali, Alexandra, Rosovsky, Rachel, Turbini, Victoria, Wood, Valerie, Al-Samkari, Hanny, Pipe, Steven, Weyand, Angela, Shavit, Jordan, Soni, Amit, Nugent, Diane, Hwang, Nina, Salinas, Vanessa, Young, Guy, Hofstra, Tom, Donkin, Jennifer, Keegan, Jacquelyn, Sibgha, Zaheer, Leung, Wendy, Jaffray, Julie, Pipe, Steven W. ⁷, Menapace, Laurel A. ¹⁷, Zhang, Chuanwu ¹⁸, Shen, Yuqian ¹⁹, Puurunen, Marja ¹⁷, Demissie, Marek ¹⁷

Source: In Blood February 2025

Systematic search for the UBA1 mutation in men after a first episode of venous thromboembolism: A monocentric study

Authors: Khider, Lina, Templé, Marie, Bally, Cécile, Spaeth, Agathe, Darnige, Luc, Sanchez, Olivier, Planquette, Benjamin, Mortelette, Hélène, Messas, Emmanuel, Smadja, David M., Emmerich, Joseph, Mirault, Tristan, Kosmider, Olivier, Gendron, Nicolas ^*

Source: In Journal of Thrombosis and Haemostasis November 2022 20(11):2697-2699

Systematic search for the UBA1 mutation in men after a first venous thrombotic episode

Authors: Khider, Lina, Templé, Marie, Bally, Cecile, Spaeth, Agathe, Darnige, Luc, Sanchez, Olivier, Planquette, Benjamin, Messas, Emmanuel, Smadja, David, Emmerich, Joseph, Mirault, Tristan, Kosmider, Olivier, Gendron, Nicolas

Source: Archives of cardiovascular diseases.Supplements. 15(2):182-183

Availability: http://explore.bl.uk/primo_library/libweb/action/display.do?tabs=detailsTab&gathStatTab=true&ct=display&fn=search&doc=ETOCvdc_100191445502.0x000001&indx=1&recIds=ETOCvdc_100191445502.0x000001

Comparison of TP53 mutations screening by functional assay of separated allele in yeast and next-generation sequencing in myelodysplastic syndromes

Authors: Bally, Cécile, Renneville, Aline, Preudhomme, Claude, Legrand, M., Adès, Lionel, de Thé, Hugues, Fenaux, Pierre, Lehmann-Che, Jacqueline

Source: In Leukemia Research November 2015 39(11):1214-1219

Prognostic value of TP53 gene mutations in myelodysplastic syndromes and acute myeloid leukemia treated with azacitidine

Authors: Bally, Cecile, Adès, Lionel, Renneville, Aline, Sebert, Marie, Eclache, Virginie, Preudhomme, Claude, Mozziconacci, Marie-Joelle, de The, Hugues, Lehmann-Che, Jacqueline, Fenaux, Pierre

Source: In Leukemia Research July 2014 38(7):751-755

Interferences by factor VIII and lupus anticoagulant in the modified one‐stage assay for emicizumab.

Authors: Habay, Capucine, Auditeau, Claire, Blandinières, Adeline, Bentounes, Nûn K, Lavenu‐Bombled, Cécile, Harroche, Annie, Bally, Cecile, Frenzel, Laurent, Borgel, Delphine, Lasne, Dominique

Source: Haemophilia; Nov2023, Vol. 29 Issue 6, p1661-1664, 4p

Subject Terms: BLOOD coagulation factor VIII, EMICIZUMAB, PARTIAL thromboplastin time, MONOCLONAL antibodies

Azacitidine in the treatment of therapy related myelodysplastic syndrome and acute myeloid leukemia (tMDS/AML): A report on 54 patients by the Groupe Francophone Des Myelodysplasies (GFM)

Authors: Bally, Cecile, Thépot, Sylvain, Quesnel, Bruno, Vey, Norbert, Dreyfus, Francois, Fadlallah, Jehane, Turlure, Pascal, de Botton, Stephane, Dartigeas, Caroline, de Renzis, Benoit, Itzykson, Raphael, Fenaux, Pierre, Adès, Lionel

Source: In Leukemia Research June 2013 37(6):637-640

Transfusion independence after lenalidomide discontinuation in patients with del(5q) myelodysplastic neoplasm: a HARMONY Alliance study

Authors: Crisà, Elena, Mora, Elvira, Germing, Ulrich, Bally, Cecile, Diez Campelo, Maria, Myllymäki, Mikko, Jädersten, Martin, Komrokji, Rami, Platzbecker, Uwe, Haase, Detlef, Hofmann, Wolf-Karsten, Al Ali, Najla H., Barraco, Daniela, Bargay, Juan José, Bernal, Teresa, López Cadenas, Felix, Calvisi, Anna, Capodanno, Isabella, Cerrano, Marco, Ciancia, Rosanna, Crugnola, Monica, Kündgen, Andrea, Finelli, Carlo, Fozza, Claudio, Frairia, Chiara, Freja, Ebeling, Ganster, Christina, Kubasch, Anne Sophie, Jimenez, Maria Jose, Latagliata, Roberto, Hernandez Mohedo, Francisca, Molero, Antonieta, Vara Pampliega, Miriam, Perez, Clara Aparicio, Pietrantuono, Giuseppe, Poloni, Antonella, Pomares, Helena, Recasens, Valle, Rüfer, Axel, Signori, Alessio, Hellstrom-Lindberg, Eva, Fenaux, Pierre, Sanz, Guillermo, Santini, Valeria

Source: Leukemia; 20240101, Issue: Preprints p1-7, 7p

Recherche systématique de la mutation UBA1 chez les hommes après un premier épisode thrombotique veineux

Authors: Khider, Lina, Templé, Marie, Bally, Cécile, Spaeth, Agathe, Darnige, Luc, Sanchez, Olivier, Planquette, Benjamin, Mortelette, Hélène, Messas, Emmanuel, Smadja, David M., Emmerich, Joseph, Mirault, Tristan, Kosmider, Olivier, Gendron, Nicolas

Source: In JMV-Journal de Médecine Vasculaire March 2023 48 Supplement:S55-S55

Ivosidenib Monotherapy Is Effective in Patients with IDH1 Mutated Myelodysplastic Syndrome (MDS): The Idiome Phase 2 Study By the GFM Group

Authors: Sebert, Marie, Cluzeau, Thomas, Beyne Rauzy, Odile, Stamatoulas Bastard, Aspasia, Dimicoli-Salazar, Sophie, Thepot, Sylvain, Peterlin, Pierre, Park, Sophie, Gourin, Marie-Pierre, Brehar, Oana, Bally, Cécile, Maury, Sébastien, Fossard, Gaelle, Ait Si Selmi, Lamya, Chaffaut, Cendrine, Clappier, Emmanuelle, Itzykson, Raphael, Chermat, Fatiha, Chevret, Sylvie, Fenaux, Pierre, Ades, Lionel

Source: In Blood 23 November 2021 138 Supplement 1:62-62

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Current Treatments Do Not Improve the Prognosis of Patients with Atypical CML and Unclassified MDS/MPN. a Joint Report from Fi-LMC, FIM, Gfch and GFM

Authors: Julien, Vaidie ^*, Rea, Delphine, Thepot, Sylvain ^*, Bruno, Le Pluart ^*, Gachard, Nathalie ^*, Struski, Stéphanie ^*, Roy, Lydia ^*, Bally, Cecile ^*, Caers, Jo ^*, Nicolini, Franck E, Cassinat, Bruno ^*, Lippert, Eric ^*, Legros, Laurence ^*, Itzykson, Raphael

Source: In Blood 13 November 2019 134 Supplement 1:2954-2954

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Outcome of NPM1 Mutated Acute Myeloid Leukemia (AML) Treated with Hypomethylating Agents (HMAs): A Report on 71 Cases

Authors: Prata, Pedro H, Bally, Cecile ^*, Prebet, Thomas, Recher, Christian, Venton, Geoffroy ^*, Thomas, Xavier, Raffoux, Emmanuel ^*, Pigneux, Arnaud ^*, Cluzeau, Thomas, Desoutter, Judith ^*, Gay, Julie ^*, Preudhomme, Claude, Fenaux, Pierre, Ades, Lionel ^*

Source: In Blood 8 December 2017 130 Supplement 1:1335-1335

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