Novel lentiviral vectors for gene therapy of sickle cell disease combining gene addition and gene silencing strategies

Authors: Brusson, Mégane, Chalumeau, Anne, Martinucci, Pierre, Romano, Oriana, Felix, Tristan, Poletti, Valentina, Scaramuzza, Samantha, Ramadier, Sophie, Masson, Cecile, Ferrari, Giuliana, Mavilio, Fulvio, Cavazzana, Marina, Amendola, Mario, Miccio, Annarita

Source: Molecular therapy.Nucleic acids. 32:229-246

Availability: http://explore.bl.uk/primo_library/libweb/action/display.do?tabs=detailsTab&gathStatTab=true&ct=display&fn=search&doc=ETOCvdc_100194168261.0x000001&indx=1&recIds=ETOCvdc_100194168261.0x000001

Combination of lentiviral and genome editing technologies for the treatment of sickle cell disease

Authors: Ramadier, Sophie, Chalumeau, Anne, Felix, Tristan, Othman, Nadia, Aknoun, Sherazade, Casini, Antonio, Maule, Giulia, Masson, Cecile, De Cian, Anne, Frati, Giacomo, Brusson, Megane, Concordet, Jean-Paul, Cavazzana, Marina, Cereseto, Anna, El Nemer, Wassim, Amendola, Mario, Wattellier, Benoit, Meneghini, Vasco, Miccio, Annarita

Source: Molecular therapy. 30(1):145-163

Availability: http://explore.bl.uk/primo_library/libweb/action/display.do?tabs=detailsTab&gathStatTab=true&ct=display&fn=search&doc=ETOCvdc_100170949958.0x000001&indx=1&recIds=ETOCvdc_100170949958.0x000001

A combination of cyclophosphamide and interleukin-2 allows CD4+ T cells converted to Tregs to control scurfy syndrome

Authors: Delville, Marianne ^*, Bellier, Florence, Leon, Juliette, Klifa, Roman, Lizot, Sabrina, Vinçon, Hélène, Sobrino, Steicy, Thouenon, Romane, Marchal, Armance, Garrigue, Alexandrine, Olivré, Juliette, Charbonnier, Soëli, Lagresle-Peyrou, Chantal, Amendola, Mario, Schambach, Axel, Gross, David, Lamarthée, Baptiste, Benoist, Christophe, Zuber, Julien, André, Isabelle ^*, Cavazzana, Marina ^*, Six, Emmanuelle ^*

Source: In Blood 29 April 2021 137(17):2326-2336

Correction of β-thalassemia by CRISPR/Cas9 editing of the α-globin locus in human hematopoietic stem cells

Authors: Pavani, Giulia, Fabiano, Anna ^*, Laurent, Marine ^*, Amor, Fatima, Cantelli, Erika, Chalumeau, Anne, Maule, Giulia, Tachtsidi, Alexandra, Concordet, Jean-Paul, Cereseto, Anna, Mavilio, Fulvio, Ferrari, Giuliana, Miccio, Annarita, Amendola, Mario

Source: In Blood Advances 9 March 2021 5(5):1137-1153

Recent Progress in Genome Editing for Gene Therapy Applications: The French Perspective

Authors: Amendola, Mario, Bedel, Aurélie, Buj-Bello, Ana, Carrara, Mathieu, Concordet, Jean-Paul, Frati, Giacomo, Gilot, David, Giovannangeli, Carine, Gutierrez-Guerrero, Alejandra, Laurent, Marine, Miccio, Annarita, Moreau-Gaudry, François, Sourd, Célia, Valton, Julien, Verhoeyen, Els

Source: Human gene therapy. 32(19/20):1059-1075

Availability: http://explore.bl.uk/primo_library/libweb/action/display.do?tabs=detailsTab&gathStatTab=true&ct=display&fn=search&doc=ETOCvdc_100132323918.0x000001&indx=1&recIds=ETOCvdc_100132323918.0x000001

GATA Factor-Mediated Gene Regulation in Human Erythropoiesis

Authors: Romano, Oriana, Petiti, Luca, Felix, Tristan, Meneghini, Vasco, Portafax, Michel, Antoniani, Chiara, Amendola, Mario, Bicciato, Silvio, Peano, Clelia, Miccio, Annarita

Source: In iScience 24 April 2020 23(4)

Optimization of CRISPR/Cas9 Delivery to Human Hematopoietic Stem and Progenitor Cells for Therapeutic Genomic Rearrangements

Authors: Lattanzi, Annalisa, Meneghini, Vasco, Pavani, Giulia, Amor, Fatima, Ramadier, Sophie, Felix, Tristan, Antoniani, Chiara, Masson, Cecile, Alibeu, Olivier, Lee, Ciaran, Porteus, Matthew H., Bao, Gang, Amendola, Mario, Mavilio, Fulvio, Miccio, Annarita

Source: In Molecular Therapy 2 January 2019 27(1):137-150

Induction of fetal hemoglobin synthesis by CRISPR/Cas9-mediated editing of the human β-globin locus

Authors: Antoniani, Chiara ^*, Meneghini, Vasco ^*, Lattanzi, Annalisa, Felix, Tristan, Romano, Oriana, Magrin, Elisa, Weber, Leslie, Pavani, Giulia, El Hoss, Sara, Kurita, Ryo, Nakamura, Yukio, Cradick, Thomas J., Lundberg, Ante S., Porteus, Matthew, Amendola, Mario, El Nemer, Wassim, Cavazzana, Marina, Mavilio, Fulvio, Miccio, Annarita

Source: In Blood 26 April 2018 131(17):1960-1973

Technological Shocks and the Conduct of Monetary Policy

Authors: Amendola, Mario, Gaffard, Jean-Luc, Saraceno, Francesco

Source: Revue économique, 2004 Nov 01. 55(6), 1241-1263.

Access URL: https://www.jstor.org/stable/3503352

The Cohesin Release Factor WAPL Restricts Chromatin Loop Extension

Authors: Haarhuis, Judith H.I., van der Weide, Robin H., Blomen, Vincent A., Yáñez-Cuna, J. Omar, Amendola, Mario, van Ruiten, Marjon S., Krijger, Peter H.L., Teunissen, Hans, Medema, René H., van Steensel, Bas, Brummelkamp, Thijn R., de Wit, Elzo, Rowland, Benjamin D.

Source: In Cell 4 May 2017 169(4):693-707

Genome-wide Maps of Nuclear Lamina Interactions in Single Human Cells

Authors: Kind, Jop, Pagie, Ludo, de Vries, Sandra S., Nahidiazar, Leila, Dey, Siddharth S., Bienko, Magda, Zhan, Ye, Lajoie, Bryan, de Graaf, Carolyn A., Amendola, Mario, Fudenberg, Geoffrey, Imakaev, Maxim, Mirny, Leonid A., Jalink, Kees, Dekker, Job, van Oudenaarden, Alexander, van Steensel, Bas

Source: In Cell 24 September 2015 163(1):134-147

Mechanisms and dynamics of nuclear lamina–genome interactions

Authors: Amendola, Mario, van Steensel, Bas

Source: In Current Opinion in Cell Biology June 2014 28:61-68

Time to build and out-of-equilibrium growth process

Authors: Amendola, Mario, Gaffard, Jean-Luc

Source: In Structural Change and Economic Dynamics June 2014 29:19-27

Competition and Increasing Returns

Authors: Amendola, Mario, Gaffard, Jean-Luc

Source: Jahrbücher für Nationalökonomie und Statistik / Journal of Economics and Statistics, 2014 Apr 01. 234(2/3), 257-273.

Access URL: https://www.jstor.org/stable/24614939

A Double-Switch Vector System Positively Regulates Transgene Expression by Endogenous microRNA Expression (miR-ON Vector)

Authors: Amendola, Mario, Giustacchini, Alice, Gentner, Bernhard, Naldini, Luigi

Source: In Molecular Therapy May 2013 21(5):934-946

Ex vivo editing of human hematopoietic stem cells for erythroid expression of therapeutic proteins

Authors: Pavani, Giulia, Laurent, Marine, Fabiano, Anna, Cantelli, Erika, Sakkal, Aboud, Corre, Guillaume, Lenting, Peter J., Concordet, Jean-Paul, Toueille, Magali, Miccio, Annarita, Amendola, Mario

Source: Nature communications. 11(1)

Availability: http://explore.bl.uk/primo_library/libweb/action/display.do?tabs=detailsTab&gathStatTab=true&ct=display&fn=search&doc=ETOCvdc_100174555580.0x000001&indx=1&recIds=ETOCvdc_100174555580.0x000001

Author Correction: Ex vivo editing of human hematopoietic stem cells for erythroid expression of therapeutic proteins

Authors: Pavani, Giulia, Laurent, Marine, Fabiano, Anna, Cantelli, Erika, Sakkal, Aboud, Corre, Guillaume, Lenting, Peter J., Concordet, Jean-Paul, Toueille, Magali, Miccio, Annarita, Amendola, Mario

Source: Nature communications. 11(1)

Availability: http://explore.bl.uk/primo_library/libweb/action/display.do?tabs=detailsTab&gathStatTab=true&ct=display&fn=search&doc=ETOCvdc_100174532124.0x000001&indx=1&recIds=ETOCvdc_100174532124.0x000001

Single-Cell Dynamics of Genome-Nuclear Lamina Interactions

Authors: Kind, Jop, Pagie, Ludo, Ortabozkoyun, Havva, Boyle, Shelagh, de Vries, Sandra S., Janssen, Hans, Amendola, Mario, Nolen, Leisha D., Bickmore, Wendy A., van Steensel, Bas

Source: In Cell 28 March 2013 153(1):178-192

Oxidative stress and cell death in cells expressing L-ferritin variants causing neuroferritinopathy

Authors: Cozzi, Anna, Rovelli, Elisabetta, Frizzale, Grazia, Campanella, Alessandro, Amendola, Mario, Arosio, Paolo, Levi, Sonia

Source: In Neurobiology of Disease January 2010 37(1):77-85

Complémentarité intertemporelle de la production, coordination de l'activité économique et croissance hors de l'équilibre

Authors: Amendola, Mario, Gaffard, Jean-Luc

Source: Revue économique, 1995 Nov 01. 46(6), 1527-1540.

Access URL: https://www.jstor.org/stable/3502461