Allogeneic haematopoietic stem-cell transplantation for children with refractory systemic juvenile idiopathic arthritis and associated lung disease: outcomes from an international, retrospective cohort study

Authors: Matt, Michael G ^{a, *}, Drozdov, Daniel ^{b, g, h, *}, Bendstrup, Elisabeth ^j, Glerup, Mia ^k, Hauge, Ellen-Margrethe ^l, Masmas, Tania ^m, Schneider, Elvira Cannizzaro ⁱ, Zeilhofer, Ulrike B ^h, Abu-Arja, Rolla F ⁿ, Driest, Kyla D ^o, Oved, Joseph H ^p, Onel, Karen ^q, Ebens, Christen L ^r, Chellapandian, Deepakbabu ^s, Chandrakasan, Shanmuganathan ^t, Prahalad, Sampath ^t, Roth, Johannes ^{u, v}, Prockop, Susan E ^w, Silva, Juliana ^x, Schapiro, Andrew H ^{c, e, f}, Towe, Christopher ^{d, f}, Chandra, Sharat ^{b, f}, Grom, Alexei ^{a, f}, Schulert, Grant S ^{a, f, †, *}, Marsh, Rebecca A ^{b, f, y, †, **}

Source: In The Lancet Rheumatology April 2025 7(4):e243-e251

Tabelecleucel for EBV+ PTLD after allogeneic HCT or SOT in a multicenter expanded access protocol

Authors: Nikiforow, Sarah, Whangbo, Jennifer S., Reshef, Ran, Tsai, Donald E., Bunin, Nancy, Abu-Arja, Rolla, Mahadeo, Kris Michael, Weng, Wen-Kai, Van Besien, Koen, Loeb, David, Nasta, Sunita Dwivedy, Nemecek, Eneida R., Zhao, Weizhi, Sun, Yan, Galderisi, Faith, Wahlstrom, Justin, Mehta, Aditi, Gamelin, Laurence, Dinavahi, Rajani, Prockop, Susan

Source: In Blood Advances 25 June 2024 8(12):3001-3012

Allogeneic Hematopoietic Stem Cell Transplantation in Immunodeficiency—Centromeric Instability—Facial Dysmorphism (ICF) Syndrome: an EBMT/ESID Inborn Errors Working Party Study.

Authors: Berghuis, Dagmar, Mehyar, Lubna S., Abu-Arja, Rolla, Albert, Michael H., Barnum, Jessie L., von Bernuth, Horst, Elfeky, Reem, Lewalle, Philippe, Laberko, Alexandra, Ghosh, Sujal, Slatter, Mary A., Weemaes, Corry M. R., Yesilipek, Akif, Sirait, Tiarlan, Neven, Bénédicte, Gennery, Andrew R., Lankester, Arjan C.

Source: Journal of Clinical Immunology; Dec2024, Vol. 44 Issue 8, p1-18, 18p

Excellent outcomes following hematopoietic cell transplantation for Wiskott-Aldrich syndrome: a PIDTC report

Authors: Burroughs, Lauri M. ^{1, 1, 2}, Petrovic, Aleksandra ^{1, 2}, Brazauskas, Ruta ³, Liu, Xuerong ³, Griffith, Linda M. ⁴, Ochs, Hans D. ², Bleesing, Jack J. ⁵, Edwards, Stephanie ⁵, Dvorak, Christopher C. ⁶, Chaudhury, Sonali ⁷, Prockop, Susan E. ⁸, Quinones, Ralph ⁹, Goldman, Frederick D. ¹⁰, Quigg, Troy C. ¹¹, Chandrakasan, Shanmuganathan ¹², Smith, Angela R. ¹³, Parikh, Suhag ¹⁴, Dávila Saldaña, Blachy J. ¹⁵, Thakar, Monica S. ¹⁶, Phelan, Rachel ¹⁶, Shenoy, Shalini ¹⁷, Forbes, Lisa R. ¹⁸, Martinez, Caridad ¹⁹, Chellapandian, Deepak ²⁰, Shereck, Evan ²¹, Miller, Holly K. ²², Kapoor, Neena ²³, Barnum, Jessie L. ²⁴, Chong, Hey ²⁴, Shyr, David C. ²⁵, Chen, Karin ²⁶, Abu-Arja, Rolla ²⁷, Shah, Ami J. ²⁸, Weinacht, Katja G. ²⁸, Moore, Theodore B. ²⁹, Joshi, Avni ³⁰, DeSantes, Kenneth B. ³¹, Gillio, Alfred P. ³², Cuvelier, Geoffrey D.E. ³³, Keller, Michael D. ^{34, 35}, Rozmus, Jacob ³⁶, Torgerson, Troy ², Pulsipher, Michael A. ²³, Haddad, Elie ³⁷, Sullivan, Kathleen E. ³⁸, Logan, Brent R. ³, Kohn, Donald B. ²⁹, Puck, Jennifer M. ⁶, Notarangelo, Luigi D. ³⁹, Pai, Sung-Yun ^{40, 41, *}, Rawlings, David J. ^{2, *}, Cowan, Morton J. ^{6, *}

Source: In Blood 4 June 2020 135(23):2094-2105

Refractory Thrombocytopenia Is a Valid Early Diagnostic Criteria for Hepatic Veno-Occlusive Disease in Children

Authors: Embaby, Mostafa M., Rangarajan, Hemalatha G., Abu-Arja, Rolla, Auletta, Jeffery J., Stanek, Joseph, Pai, Vinita, Nicol, Kathleen K., Bajwa, Rajinder S.

Source: In Biology of Blood and Marrow Transplantation March 2020 26(3):546-552

Increased Health Care Utilization and Costs during Allogeneic Hematopoietic Cell Transplantation for Acute Leukemia and Myelodysplastic Syndromes in Adolescents and Young Adults Compared with Children: A Multicenter Study

Authors: Rangarajan, Hemalatha G., Smith, Lauren C., Stanek, Joseph R., Hall, Matthew, Abu-Arja, Rolla, Auletta, Jeffery J., O'Brien, Sarah H.

Source: In Biology of Blood and Marrow Transplantation May 2019 25(5):1031-1038

Venous Thromboembolism in Pediatric Hematopoietic Cell Transplant: A Multicenter Cohort Study

Authors: Rangarajan, Hemalatha G. ^*, Stanek, Joseph R., Abu-Arja, Rolla, Bajwa, Rajinder P.S., Auletta, Jeffery J., Lee, Dean A., O'Brien, Sarah H., Kumar, Riten

Source: In Biology of Blood and Marrow Transplantation February 2018 24(2):337-342

Hematopoietic Cell Transplantation for Congenital Dyserythropoietic Anemia: A Report from the Pediatric Transplant and Cellular Therapy Consortium

Authors: Rangarajan, Hemalatha G., Stanek, Joseph R., Abdel-Azim, Hisham, Modi, Arunkumar, Haight, Ann, McKinney, Christopher M., McKeone, Daniel J., Buchbinder, David K., Katsanis, Emmanuel, Abusin, Ghada A., Ahmed, Ibrahim, Law, Jason, Silva, Jorge Galvez, Mallhi, Kanwaldeep K., Burroughs, Lauri M., Shah, Niketa, Shaw, Peter J., Greiner, Robert, Shenoy, Shalini, Pulsipher, Michael A., Abu-Arja, Rolla

Source: In Transplantation and Cellular Therapy June 2022 28(6):329-329

Acute kidney injury in pediatric hematopoietic cell transplantation: critical appraisal and consensus.

Authors: Raina, Rupesh^1,2 rraina@akronchildrens.org, Abu-Arja, Rolla^3,4, Sethi, Sidharth⁵, Dua, Richa⁶, Chakraborty, Ronith¹, Dibb, James T.⁷, Basu, Rajit K.⁸, Bissler, John⁹, Felix, Melvin Bonilla¹⁰, Brophy, Patrick¹¹, Bunchman, Timothy¹², Alhasan, Khalid¹³, Haffner, Dieter¹⁴, Kim, Yap Hui^15,16, Licht, Christopher¹⁷, McCulloch, Mignon¹⁸, Menon, Shina¹⁹, Onder, Ali Mirza^20,21, Khooblall, Prajit²², Khooblall, Amrit¹

Source: Pediatric Nephrology. Jun2022, Vol. 37 Issue 6, p1179-1203. 25p. 2 Color Photographs, 6 Charts, 2 Graphs.

Subject Terms: *CONSENSUS (Social sciences), *ONLINE information services, *MEDICAL databases, *CONFIDENCE intervals, *MEDICAL information storage & retrieval systems, *META-analysis, *SYSTEMATIC reviews, *CARCINOGENESIS, *PEDIATRICS, *METABOLIC disorders, *DESCRIPTIVE statistics, *HEMATOPOIETIC stem cells, *ODDS ratio, *MEDLINE, *DATA analysis software, *ACUTE kidney failure, *CELL transplantation, *DISEASE risk factors

Isolated Optic Nerve Relapse in a Pediatric Patient With T-Cell Lymphoblastic Leukemia: A Brief Report.

Authors: Shenkar, Rakefet, Kahwash, Samir B., Rodriguez, Diana P., Abu Arja, Rolla, Reed, Suzanne M., Rangarajan, Hemalatha G.

Source: Journal of Pediatric Hematology/Oncology; Aug2024, Vol. 46 Issue 6, pe443-e447, 5p

Tabelecleucel for EBV+PTLD after allogeneic HCT or SOT in a multicenter expanded access protocol

Authors: Nikiforow, Sarah, Whangbo, Jennifer S., Reshef, Ran, Tsai, Donald E., Bunin, Nancy, Abu-Arja, Rolla, Mahadeo, Kris Michael, Weng, Wen-Kai, Van Besien, Koen, Loeb, David, Nasta, Sunita Dwivedy, Nemecek, Eneida R., Zhao, Weizhi, Sun, Yan, Galderisi, Faith, Wahlstrom, Justin, Mehta, Aditi, Gamelin, Laurence, Dinavahi, Rajani, Prockop, Susan

Source: Blood Advances; June 2024, Vol. 8 Issue: 12 p3001-3012, 12p

An International Survey of Allogeneic Hematopoietic Cell Transplantation for X-Linked Agammaglobulinemia.

Authors: Nishimura, Akira, Uppuluri, Ramya, Raj, Revathi, Swaminathan, Venkateswaran Vellaichamy, Cheng, Yifei, Abu-Arja, Rolla F., Fu, Bin, Laberko, Alexandra, Albert, Michael H., Hauck, Fabian, Bucciol, Giorgia, Bigley, Venetia, Elcombe, Suzanne, Kharya, Gaurav, Pronk, Cornelis Jan H, Wehr, Claudia, Neven, Bénédicte, Warnatz, Klaus, Meyts, Isabelle, Morio, Tomohiro

Source: Journal of Clinical Immunology; Nov2023, Vol. 43 Issue 8, p1827-1839, 13p

Subject Terms: HEMATOPOIETIC stem cell transplantation, AGAMMAGLOBULINEMIA, BRUTON tyrosine kinase

Long term survivor of MOZ-p300 therapy-related acute myeloid leukemia after matched unrelated donor bone marrow transplantation.

Authors: Mehyar, Lubna S, Hartog, Leigh, Kahwash, Samir B., Abu-Arja, Rolla, Ranalli, Mark, Rangarajan, Hemalatha G.

Source: Leukemia & Lymphoma; Jul2023, Vol. 64 Issue 7, p1344-1347, 4p

Subject Terms: ACUTE myeloid leukemia, BONE marrow transplantation, HEPATIC veno-occlusive disease, ZINC-finger proteins, NEUROBLASTOMA, EXTRAMEDULLARY diseases, CHRONIC leukemia

Impact of Modification of Immunosuppressive Therapy Following Diagnosis of Transplant-Associated Thrombotic Microangiopathy in Allogeneic Hematopoietic Stem Cell Transplant Recipients: A Single Center Experience

Authors: Rush, Cassandra E, Stanek, Joseph, Bajwa, Rajinder PS, Lamb, Margaret, Abu-Arja, Rolla, Rangarajan, Hemalatha G.

Source: In Transplantation and Cellular Therapy February 2024 30(2) Supplement:S137-S138

Adenoviral Cellular Therapy with Adenovirus (ADV)-Specific Cytotoxic T-Lymphocytes (CTLs) for Resistant Infections in Children, Adolescent, and Young Adult (CAYA) Patients Following Allogeneic Hematopoietic Stem Cell Transplantation (AlloHSCT): A Promising Approach

Authors: Schaefer, Edo, Vu, Christine, Flower, Allyson, Ayello, Janet, Chu, Yaya, van de Ven, Carmella, Mintzer, Elizabeth, Harrison, Lauren, Morris, Erin, Wang, Yongping, Shenoy, Shalini, Lee, Dean Anthony, Abu-Arja, Rolla, Johnson, Bryon D, Verneris, Michael R., Dvorak, Christopher C., Chu, Julia, Cooke, Kenneth R., Talano, Julie A, Bunin, Nancy J., Cairo, Mitchell S.

Source: In Transplantation and Cellular Therapy February 2024 30(2) Supplement:S432-S432

Assessing Post-Transplant Outcomes in Hematopoietic Stem Cell Recipients from Rural, Appalachian, and Medically Underserved Regions: Insights from a Single-Center Investigation

Authors: Kuns, Olivia, Stanek, Joseph, Olsavsky, Anna, Ralph, Jessica, Franklin, Bianca, Abu-Arja, Rolla, Skeens, Micah A

Source: In Transplantation and Cellular Therapy February 2024 30(2) Supplement:S334-S334

Real World Experience on the Use of Vedolizumab for Treatment of Steroid Refractory Lower Gastrointestinal Acute Graft Versus Host Disease in Pediatric Allogeneic Stem Cell Transplant Recipients: A Multicenter Study

Authors: Bowman, Sara, John, Tami, Morales, Erin A, Phelan, Rachel, Schmeling, Kristine, Lust, Hannah, Yanik, Gregory A., Abu-Arja, Rolla, Stanek, Joseph, Milner, Jordan, Horn, Biljana, Rangarajan, Hemalatha G.

Source: In Transplantation and Cellular Therapy February 2024 30(2) Supplement:S94-S94

Costs of Cord Blood Transplantation Are Higher Than Other Graft Sources in Patients with Acute Leukemia and Myelodysplastic Syndrome Treated at Pediatric Centers

Authors: Rangarajan, Hemalatha G., Stanek, Joseph R., Abu-Arja, Rolla

Source: In Biology of Blood and Marrow Transplantation December 2020 26(12):e313-e315

Safety and Efficacy of Virus-Specific Cytotoxic T-Lymphocytes Manufactured By the IFN-g Cytokine Capture System for the Treatment of Refractory Adenovirus, Cytomegalovirus, Epstein Barr Virus, and BK Virus Infections in Children, Adolescents and Young Adults after Allogeneic Hematopoietic Stem Cell Transplantation, Solid Organ Transplantation, or with Primary Immunodeficiency (IND# 17449)

Authors: Flower, Allyson M. ^*, Friedmann, Rachel ^*, Ayello, Janet ^*, Rigot, Olivia ^*, Harrison, Lauren ^*, Morris, Erin ^*, Sturhahn, Meghan ^*, Maryamchik, Elana ^*, Wang, Yongping ^*, O'Donnell, Lynn ^*, Abu-Arja, Rolla ^*, Lee, Dean Anthony, Talano, Julie-An, Johnson, Bryon, Bunin, Nancy, Cairo, Mitchell S

Source: In Blood 5 November 2020 136 Supplement 1:2-4

Part 5: Allogeneic HSCT in refractory SJIA with lung disease; recent cases from centers in North America & Europe.

Authors: Grom, Alexei A., Canna, Scott W., Abu-Arja, Rolla F., Sinha, Rashmi, Peixoto, Luciana, Cannizzaro, Elvira, Chandrakasan, Shanmuganathan, Driest, Kyla, Marsh, Rebecca, Neven, Bénédicte, Onel, Karen, Prahalad, Sampath, Prockop, Susan, Quartier, Pierre, Roth, Johannes, Schulert, Grant, Silva, Juliana M.F., Wall, Donna, Zeilhofer, Ulrike

Source: Pediatric Rheumatology; 1/5/2023, Vol. 21 Issue 1, p1-13, 13p

Subject Terms: HEMATOPOIETIC stem cell transplantation, LUNG diseases, REFRACTORY materials

Geographic Terms: NORTH America